| Name |
Years |
Research Subject |
| Leonard Sender (MD) |
1988-1989 |
Glucocerebrosidase (GC) gene expression |
| Joel Weinthal (MD) |
1989-1991 |
GC gene expression in murine bone marrow |
| Gay M. Crooks (MD) |
1991-1993 |
Gene transfer to human hematopoietic stem cells |
| Wanda J. Krall (PhD) |
1993-1995 |
Regulation of gene from retroviral vectors |
| Jan A. Nolta (PhD) |
1994-1996 |
Gene transfer into human stem cells |
| Punam Malik (MD) |
1995-1997 |
Lineage-directed gene expression, AAV |
| Mei-Mei Huang (PhD) |
1995-1997 |
Gene therapy for Hurler disease, Wiskott-Aldrich |
| Robert Cooper (MD) |
1995-1997 |
Role of methylation in vector silencing |
| Leo Mascarenhas (MD) |
1996-1998 |
Gene transfer into human leukemia cells |
| Renata Stripecke (PhD) |
1995-1999 |
Immunotherapy of childhood leukemia |
| Stephanie Halene (MD) |
1997–2000 |
Vector expression/silencing |
| Scott Case (PhD) |
1997–2000 |
Lentiviral vectors for gene therapy |
| Steve Rawlings (PhD) |
1999–2000 |
Vectors encoding HIV inducible apoptosis |
| Diana Fan (MD) |
2000 2001-2002 |
Immunotherapy for childhood leukemia |
| Noriko Satake (MD) |
1998–2001 |
Immune responses and tolerance to transgenes |
| Barbara Engel (MD) |
1998–2001 |
HIV gene therapy |
| Carolyn Lutzko (PhD) |
1999–2004 |
Lineage specific gene expression |
| Hiroshi Kobayashi (MD) |
2002–2004 |
Gene therapy for lysosomal storage disease |
| Kit Shaw (PhD) |
2002–2007 |
Lineage specific gene expression |
| Roger Hollis (PhD) |
2003–2006 |
Gene transfer to human hematopoietic stem cells |
| Christof Kahl (PhD) |
2003–2007 |
Gene transfer to rhesus CD34+ cells |
| Noriko Satake (MD) |
2005–2007 |
Immunotherapy of leukemia |
| Ken Sakurai (MD/PhD) |
2007–2010 |
Gene expression in human ESC |
| Satiro De Oliveira (MD) |
2008-2010 |
Immunotherapy of leukemia by myeloid effectors |
| Francesca Giannoni (PhD) |
2008-2010 |
Immunotherapy for cancer and leukemia |
| Rafael Ruiz de Assini (PhD) |
2010-2011 |
β-globin gene correction for sickle cell disease |
| Fabrizia Urbanati (PhD) |
2010-2012 |
β-globin gene correction for sickle cell disease |
| Sarah Larson (MD) |
2011-2013 |
Immunotherapy for Leukemia |
| Zulema Romero-Garcia (PhD) |
2010 -2014 |
Gene therapy for sickle cell disease |
| Kismet Baldwin (MD) |
2011 – 2014 |
Gene transfer to human HSC |
| Caroline Kuo (MD) |
2012 – 2014 |
Correction of the CD154 gene for X-HIM |
| Gavin Roach (MD) |
2012 – 2014 |
Clinical trial of sickle cell gene therapy |
| Carmen Bjurstroem (PhD) |
2013-2015 |
Gene editing in hematopoietic stem cells |
| Robert Drummond (MD/PhD) |
2015-2017 |
Correction of the sickle cell mutation |
| Alexandra Miggelbrink, (MD) |
2016-2017 |
CRISPR-mediated gene correction in HSC |
| Kathryn Bradford |
2018-2020 |
Gene editing for Common Variable Immune Deficiency |
| Shanna White |
2020-2022 |
Gene Therapy for Sickle Cell Disease |
